Status | Study |
Active, not recruiting |
Study Name: Efficacy and Safety of IONIS-TTR Rx in Familial Amyloid Polyneuropathy Condition: FAP Familial Amyloid Polyneuropathy Date: 2012-11-27 Interventions: Drug: IONIS-TTR Rx 300 mg IONI |
Active, not recruiting |
Study Name: Prevalence of Transthyretin Amyloidosis in Hypertrophic Cardiomyopathy Condition: Cardiac Amyloidosis Amyloidosis in Transthyretin (TTR) Hyp Date: 2012-06-13 |
Completed |
Study Name: Burden of Disease Study In Patients With Transthyretin Familial Amyloidosis Polyneuropathy (TTR-FAP) orTransthyretin Cardiomyopathy (TTR-CM) And Caregivers Condition: Transthyretin Familial Amyloidosis Polyneuropathy (TTR-FAP) Transthyretin Cardiomyopathy (TT Date: 2012-05-21 Interventions: Other: No drug No drug. |
Completed |
Study Name: Safety and Efficacy Study of Doxycycline/UrsoDeoxyCholicAcid on Disease Progression in ATTR Amyloidosis Condition: Transthyretin Amyloidosis Cardiomyopathy Date: 2012-04-19 Interventions: Drug: Doxycycline 200 mg/day ( |
Completed |
Study Name: The Effect Of Tafamidis For The Transthyretin Amyloid Polyneuropathy Patients With V30M Or Non-V30M Transthyretin Condition: Transthyretin Familial Amyloid Polyneuropathy Date: 2011-09-13 Interventions: Drug: tafamidis tafamidis meglumine 20 mg QD Other N |
Completed |
Study Name: The Effect of Diflunisal on Familial Transthyretin Amyloidosis Condition: Amyloidosis Date: 2011-09-09 Interventions: Drug: Diflunisal Film-coated tablet, 250 mg twice daily, orally for approximately 2 years |
Completed |
Study Name: Safety, Efficacy and Pharmacokinetics of Doxycycline Plus Tauroursodeoxycholic Acid in Transthyretin Amyloidosis Condition: Transthyretin Amyloidosis Date: 2010-07-27 Interventions: Drug: Doxycycline + Tauroursodeoxycholic acid doxycycline 100 mg twice a day for 12 months; tauroursodeo |
Completed |
Study Name: An Extension of Study Fx-005 Evaluating Long-Term Safety And Clinical Outcomes Of Fx-1006A In Patients With Transthyretin Amyloid Polyneuropathy Condition: Familial Amyloid Polyneuropathy ATTR-PN Date: 2008-11-13 Interventions: Drug: Fx-1006A Fx-1006A 20mg soft gelatin capsule administered orally once daily (at the same time each |
Completed |
Study Name: The Effects of Fx-1006A on Transthyretin Stabilization and Clinical Outcome Measures in Patients With Non-V30M Transthyretin Amyloidosis Condition: Transthyretin-associated Amyloidosis With Polyneuropathy Date: 2008-02-27 Interventions: Drug: Fx-1006A During Part 1, patients will receive Fx-1006A 20mg soft gelatin capsules once daily (at t |
Recruiting |
Study Name: Transthyretin-Associated Amyloidoses Outcome Survey (THAOS) Condition: Transthyretin Mutations Transthyretin Amyloidosis Date: 2008-02-25 Interventions: Other: None. Observational Study. |